市場調查報告書
商品編碼
1119090
龐貝病全球市場規模調查,按給藥途徑,按治療類型(底物減少療法,酵素替代療法,伴侶替代療法,支持性護理),用戶,地區預測 2022-2028Global Pompe Diseases Market Size study, by Route of Administration, By Treatment Type (Substrate Reduction Therapy, Enzyme Replacement Therapy, Chaperone-Advanced Replacement Therapy, Supportive Care), By End User and Regional Forecasts 2022-2028 |
2022-2028 年預測期間的 5%。
龐貝病是一種影響身體細胞中稱為糖原的複雜碳水化合物積累的疾病。它是遺傳遺傳的,會導致一些組織和器官,尤其是肌肉,積累糖原並停止正常運作。據估計,美國每 40,000 人中就有 1 人患有龐貝病。市場增長由新藥推出、長期療法的持續採用以及酵素替代療法領域的發展增加等關鍵因素推動。例如,根據 2021 年 11 月發表在 Journal of Molecules 上的一篇題為“Pharmacological Chaperone Therapy for Pompe disease”的論文,與 rhGAA 一起靜脈內給藥的酵素替代療法(ERT)是 Pompe 病的唯一治療方法。得到正式認可的。由於 ERT 的缺點,研究人員正在尋找新的治療方法,這是美國食品和藥物管理局批准的唯一藥物。此外,2021 年 8 月,酵素替代療法 Aval 葡萄糖甘酵素 Alfa 獲得美國食品藥品監督管理局 (FDA) 的批准,用於治療 1 歲及以上的遲發性龐貝病。此外,針對龐貝病的新興免疫療法將在未來幾年帶來豐厚的市場機會。然而,高昂的治療成本將阻礙 2022-2028 年預測期內的市場增長。
龐貝病全球市場研究考慮的主要地區是亞太地區、北美、歐洲、拉丁美洲和世界其他地區。由於新藥的推出和研發支出的增加,北美在整體市場份額方面處於領先地位。然而,由於患者對罕見病的認識不斷提高以及該地區龐貝病的患病率上升,預計亞太地區將增長最快。
本報告中包括的主要市場進入者是:
本研究的目的是確定近年來各個細分市場和國家/地區的市場規模,並預測未來八年的價值。本報告旨在捕捉所調查的每個地區和國家的行業的定性和定量方面。此外,它還提供了有關關鍵方面的詳細信息,例如定義市場未來增長的驅動因素和挑戰。此外,該報告還應納入微觀市場中可供利益相關者投資的可用機會,以及對競爭格局和主要參與者的應用產品的深入分析。市場的詳細細分和子細分如下所述。
按給藥途徑:
口頭
腸胃外給藥
按治療類型
底物減少療法 (SRT)
酵素替代療法 (ERT)
伴侶替代療法 (CART)
支持性護理
按最終用戶
醫院
診斷中心
門診手術中心
雜項
按地區
北美
美國
加拿大
歐洲
英國
德國
法國
西班牙
意大利
其他歐洲
亞太地區
中國
印度
日本
澳大利亞
韓國
其他亞太地區
拉丁美洲
巴西
墨西哥
世界其他地方
此外,本研究考慮的年份是:
實際年份 - 2018 年、2019 年、2020 年
2021 年基準年
預測期 - 2022 年 至 2028 年
本報告的目標受眾是全球龐貝病市場。
主要諮詢公司和顧問
大公司、中型公司、中小企業
風險投資
增值經銷商 (VAR)
第三方知識提供者
投資銀行家
投資者
Global Pompe Diseases Market is valued at approximately USD XXX million in 2021 and is anticipated to grow with a healthy growth rate of more than 4.5% over the forecast period 2022-2028. Pompe disease is a disorder affected by the buildup of a complex sugar called glycogen in the body's cells. It is inherited genetically, and the buildup of glycogen in some tissues and organs, especially muscles, makes them less able to operate normally. In the United States, one in 40,000 people have Pompe disease. The market growth is driven by key factors such as launch of novel drugs and the continued uptake of long-term therapies and increasing development in the field of enzyme replacement therapies. For instance, Enzyme replacement therapy (ERT), which involves giving rhGAA intravenously, is the only treatment for Pompe illness that has been approved, according to a paper titled "Pharmacological Chaperone Therapy for Pompe Disease" that was published in the Journal of Molecules in November 2021. Researchers are looking for novel treatments because of the shortcomings of ERT. which is the sole medication acknowledged by the US Food and Drug Administration. Furthermore, in August 2021, Enzyme Replacement therapy "Aval glucosidase Alfa" has been approved by United State of Food and Drug Administration, for the patient aged 1 year and older with late onset pompe disease. Moreover, emerging immunotherapeutic approaches for Pompe disease create lucrative opportunity for the market in upcoming years. However, high Treatment Cost impedes the growth of the market over the forecast period of 2022-2028
The key regions considered for the global Pompe Diseases Market study include Asia Pacific, North America, Europe, Latin America, and Rest of the World. North America is leading the overall market share owing to rising launches of novel drugs and growing research and development expenditure. However, Asia Pacific is expected to be the fastest growing region due to growing awareness among patients regarding rare disorders and increase in the prevalence of pompe disease in the region.
Major market players included in this report are:
Amicus Therapeutics
CENTOGENE AG
Valerion Therapeutics
Astellas Pharma
EpiVax, Inc
Oxyrane
Sanofi
AVROBIO, Inc.
Genethon
Sangamo Therapeutics
The objective of the study is to define market sizes of different segments & countries in recent years and to forecast the values to the coming eight years. The report is designed to incorporate both qualitative and quantitative aspects of the industry within each of the regions and countries involved in the study. Furthermore, the report also caters the detailed information about the crucial aspects such as driving factors & challenges which will define the future growth of the market. Additionally, the report shall also incorporate available opportunities in micro markets for stakeholders to invest along with the detailed analysis of competitive landscape and Application offerings of key players. The detailed segments and sub-segment of the market are explained below:
By Route of Administration:
Oral
Parenteral
By Treatment Type:
Substrate Reduction Therapy (SRT)
Enzyme Replacement Therapy (ERT)
Chaperone-Advanced Replacement Therapy (CART)
Supportive Care
By End User:
Hospitals
Diagnostic Centers
Ambulatory Surgical Centers
Others
By Region:
North America
U.S.
Canada
Europe
UK
Germany
France
Spain
Italy
ROE
Asia Pacific
China
India
Japan
Australia
South Korea
RoAPAC
Latin America
Brazil
Mexico
Rest of the World
Furthermore, years considered for the study are as follows:
Historical year - 2018, 2019, 2020
Base year - 2021
Forecast period - 2022 to 2028
Target Audience of the Global Pompe Diseases Market in Market Study:
Key Consulting Companies & Advisors
Large, medium-sized, and small enterprises
Venture capitalists
Value-Added Resellers (VARs)
Third-party knowledge providers
Investment bankers
Investors
List of figures