市場調查報告書

胱胺酸症 - 市場考察,流行病學,市場預測:2028年

cystinosis - Market Insight, Epidemiology and Market Forecast - 2030

出版商 DelveInsight Business Research LLP 商品編碼 923099
出版日期 內容資訊 英文 150 Pages
商品交期: 最快1-2個工作天內
價格
胱胺酸症 - 市場考察,流行病學,市場預測:2028年 cystinosis - Market Insight, Epidemiology and Market Forecast - 2030
出版日期: 2020年01月01日內容資訊: 英文 150 Pages
簡介

主要7個國家的胱胺酸症的整體市場規模在2017年估算達到1億3046萬美元。2017年∼2028年的年複合成長率預測將大幅度成長。

本報告提供全球胱胺酸症市場相關調查分析,提供疾病的背景,流行病學,主要7個國家 (美國,德國,西班牙,義大利,法國,英國,日本)的市場趨勢相關的系統性資訊。

目錄

第1章 主要考察

第2章 胱胺酸症市場概要

  • 2017年的胱胺酸症的市場佔有率分佈
  • 2028年的胱胺酸症的市場佔有率分佈

第3章 胱胺酸症:疾病的背景和概要

  • 簡介
  • 胱胺酸症的分類
  • 胱胺酸症的原因
  • 胱胺酸症的病理生理學
  • 臨床性說明和併發症
  • 胱胺酸症的遺傳的根據
  • CTNS變異的功能特性:遺傳基因型和表現型的相關
  • 診斷和生物標記的跟蹤

第4章 流行病學和患者族群

  • 主要調查結果
  • 主要7個國家的整體患者數
  • 主要7個國家的確診的整體患者數

第5章 各國胱胺酸症的流行病學

  • 美國
  • EU5個國家
  • 日本

第6章 胱胺酸症的治療和管理

  • 對症療法
  • 胱胺酸乾涸療法
  • 治療監測和預後
  • 胱胺酸症的治療指南

第7章 未滿足需求

第8章 上市藥

  • Procysbi (cysteamine bitartrate) :Horizon Pharma
  • Cystadrops (cysteamine hydrochloride) :Recordati SpA
  • Cystaran (cysteamine hydrochloride) :Leadiant Biosciences
  • Cystagon (cysteamine bitartrate) :Mylan Pharmaceuticals

第9章 新興藥

  • AVR-RD-04 (CTNS-RD-04) :Avrobio
  • ELX-02:Eloxx Pharmaceuticals
  • A0003:Mylan

第10章 胱胺酸症:主要7個國家的市場分析

  • 主要調查結果
  • 胱胺酸症的市場規模
  • 胱胺酸症的市場規模:各療法

第11章 市場預測:主要7個國家

  • 美國
  • EU5個國家
  • 日本

第12章 推動市場要素

第13章 市場障礙

第14章 SWOT分析

第15章 KOL的考察

第16章 附錄

第17章 DelveInsight的功能

第18章 免責事項

第19章 關於DelveInsight

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目錄
Product Code: DIMI0682

DelveInsight's "cystinosis - Market Insights, Epidemiology, and Market Forecast-2030" report delivers an in-depth understanding of the cystinosis, historical and forecasted epidemiology as well as the cystinosis market trends in the United States, EU5 (Germany, Spain, Italy, France, and United Kingdom) and Japan.

The cystinosis market report provides current treatment practices, emerging drugs, cystinosis market share of the individual therapies, current and forecasted cystinosis market Size from 2017 to 2030 segmented by seven major markets. The Report also covers current cystinosis treatment practice/algorithm, market drivers, market barriers and unmet medical needs to curate best of the opportunities and assesses the underlying potential of the market.

Geography Covered

  • The United States
  • EU5 (Germany, France, Italy, Spain, and the United Kingdom)
  • Japan

Study Period: 2017-2030

cystinosis Disease Understanding and Treatment Algorithm

The DelveInsight cystinosis market report gives a thorough understanding of the cystinosis by including details such as disease definition, symptoms, causes, pathophysiology, diagnosis and treatment.

Diagnosis

This segment of the report covers the detailed diagnostic methods or tests for cystinosis.

Treatment

It covers the details of conventional and current medical therapies available in the cystinosis market for the treatment of the condition. It also provides cystinosis treatment algorithms and guidelines in the United States, Europe, and Japan.

cystinosis Epidemiology

The cystinosis epidemiology division provide insights about historical and current cystinosis patient pool and forecasted trend for every seven major countries. It helps to recognize the causes of current and forecasted trends by exploring numerous studies and views of key opinion leaders. This part of the DelveInsight report also provides the diagnosed patient pool and their trends along with assumptions undertaken.

Key Findings

The disease epidemiology covered in the report provides historical as well as forecasted cystinosis epidemiology scenario in the 7MM covering the United States, EU5 countries (Germany, Spain, Italy, France, and the United Kingdom), and Japan from 2017 to 2030.

Country Wise- cystinosis Epidemiology

The epidemiology segment also provides the cystinosis epidemiology data and findings across the United States, EU5 (Germany, France, Italy, Spain, and the United Kingdom), and Japan.

cystinosis Drug Chapters

Drug chapter segment of the cystinosis report encloses the detailed analysis of cystinosis marketed drugs and late stage (Phase-III and Phase-II) pipeline drugs. It also helps to understand the cystinosis clinical trial details, expressive pharmacological action, agreements and collaborations, approval and patent details, advantages and disadvantages of each included drug and the latest news and press releases.

Marketed Drugs

The report provides the details of the marketed product available for cystinosis treatment.

cystinosis Emerging Drugs

The report provides the details of the emerging therapies under the late and mid-stage of development for cystinosis treatment.

cystinosis Market Outlook

The cystinosis market outlook of the report helps to build the detailed comprehension of the historic, current, and forecasted cystinosis market trends by analyzing the impact of current therapies on the market, unmet needs, drivers and barriers and demand of better technology.

This segment gives a thorough detail of cystinosis market trend of each marketed drug and late-stage pipeline therapy by evaluating their impact based on annual cost of therapy, inclusion and exclusion criteria's, mechanism of action, compliance rate, growing need of the market, increasing patient pool, covered patient segment, expected launch year, competition with other therapies, brand value, their impact on the market and view of the key opinion leaders. The calculated market data are presented with relevant tables and graphs to give a clear view of the market at first sight.

According to DelveInsight, cystinosis market in 7MM is expected to change in the study period 2017-2030.

Key Findings

This section includes a glimpse of the cystinosis market in 7MM.

The United States Market Outlook

This section provides the total cystinosis market size and market size by therapies in the United States.

EU-5 Countries: Market Outlook

The total cystinosis market size and market size by therapies in Germany, France, Italy, Spain, and the United Kingdom is provided in this section.

Japan Market Outlook

The total cystinosis market size and market size by therapies in Japan is also mentioned.

cystinosis Drugs Uptake

This section focusses on the rate of uptake of the potential drugs recently launched in the cystinosis market or expected to get launched in the market during the study period 2017-2030. The analysis covers cystinosis market uptake by drugs; patient uptake by therapies; and sales of each drug.

This helps in understanding the drugs with the most rapid uptake, reasons behind the maximal use of new drugs and allow the comparison of the drugs on the basis of market share and size which again will be useful in investigating factors important in market uptake and in making financial and regulatory decisions.

cystinosis Pipeline Development Activities

The report provides insights into different therapeutic candidates in Phase II, and Phase III stage. It also analyses cystinosis key players involved in developing targeted therapeutics.

Pipeline Development Activities

The report covers the detailed information of collaborations, acquisition and merger, licensing, patent details and other information for cystinosis emerging therapies.

Reimbursement Scenario in cystinosis

Approaching reimbursement proactively can have a positive impact both during the late stages of product development and well after product launch. In a report, we take reimbursement into consideration to identify economically attractive indications and market opportunities. When working with finite resources, the ability to select the markets with the fewest reimbursement barriers can be a critical business and price strategy.

KOL- Views

To keep up with current market trends, we take KOLs and SME's opinion working in cystinosis domain through primary research to fill the data gaps and validate our secondary research. Their opinion helps to understand and validate current and emerging therapies treatment patterns or cystinosis market trend. This will support the clients in potential upcoming novel treatment by identifying the overall scenario of the market and the unmet needs.

Competitive Intelligence Analysis

We perform Competitive and Market Intelligence analysis of the cystinosis Market by using various Competitive Intelligence tools that include - SWOT analysis, PESTLE analysis, Porter's five forces, BCG Matrix, Market entry strategies etc. The inclusion of the analysis entirely depends upon the data availability.

Scope of the Report

  • The report covers the descriptive overview of cystinosis, explaining its causes, signs and symptoms, pathophysiology, diagnosis and currently available therapies
  • Comprehensive insight has been provided into the cystinosis epidemiology and treatment in the 7MM
  • Additionally, an all-inclusive account of both the current and emerging therapies for cystinosis are provided, along with the assessment of new therapies, which will have an impact on the current treatment landscape
  • A detailed review of cystinosis market; historical and forecasted is included in the report, covering drug outreach in the 7MM
  • The report provides an edge while developing business strategies, by understanding trends shaping and driving the global cystinosis market

Report Highlights

  • In the coming years, cystinosis market is set to change due to the rising awareness of the disease, and incremental healthcare spending across the world; which would expand the size of the market to enable the drug manufacturers to penetrate more into the market
  • The companies and academics are working to assess challenges and seek opportunities that could influence cystinosis R&D. The therapies under development are focused on novel approaches to treat/improve the disease condition
  • Major players are involved in developing therapies for cystinosis. Launch of emerging therapies will significantly impact the cystinosis market
  • A better understanding of disease pathogenesis will also contribute to the development of novel therapeutics for cystinosis
  • Our in-depth analysis of the pipeline assets across different stages of development (Phase III and Phase II), different emerging trends and comparative analysis of pipeline products with detailed clinical profiles, key cross-competition, launch date along with product development activities will support the clients in the decision-making process regarding their therapeutic portfolio by identifying the overall scenario of the research and development activities

cystinosis Report Insights

  • Patient Population
  • Therapeutic Approaches
  • cystinosis Pipeline Analysis
  • cystinosis Market Size and Trends
  • Market Opportunities
  • Impact of upcoming Therapies

cystinosis Report Key Strengths

  • 11 Years Forecast
  • 7MM Coverage

cystinosis Epidemiology Segmentation

  • Key Cross Competition
  • Highly Analyzed Market
  • Drugs Uptake

cystinosis Report Assessment

  • Current Treatment Practices
  • Unmet Needs
  • Pipeline Product Profiles
  • Market Attractiveness
  • Market Drivers and Barriers

Key Questions

Market Insights:

  • What was the cystinosis market share (%) distribution in 2017 and how it would look like in 2030?
  • What would be the cystinosis total market size as well as market size by therapies across the 7MM during the forecast period (2017-2030)?
  • What are the key findings pertaining to the market across 7MM and which country will have the largest cystinosis market size during the forecast period (2017-2030)?
  • At what CAGR, the cystinosis market is expected to grow in 7MM during the forecast period (2017-2030)?
  • What would be the cystinosis market outlook across the 7MM during the forecast period (2017-2030)?
  • What would be the cystinosis market growth till 2030, and what will be the resultant market Size in the year 2030?
  • How would the market drivers, barriers and future opportunities affect the market dynamics and subsequent analysis of the associated trends?

Epidemiology Insights:

  • What is the disease risk, burden and unmet needs of the cystinosis?
  • What is the historical cystinosis patient pool in seven major markets covering the United States, EU5 (Germany, Spain, France, Italy, UK), and Japan?
  • What would be the forecasted patient pool of cystinosis in seven major markets covering the United States, EU5 (Germany, Spain, France, Italy, UK), and Japan?
  • What will be the growth opportunities in the 7MM with respect to the patient population pertaining to cystinosis?
  • Out of all 7MM countries, which country would have the highest prevalent population of cystinosis during the forecast period (2017-2030)?
  • At what CAGR the population is expected to grow in 7MM during the forecast period (2017-2030)?
  • Current Treatment Scenario, Marketed Drugs and Emerging Therapies:
  • What are the current options for the cystinosis treatment, along with the approved therapy?
  • What are the current treatment guidelines for the treatment of cystinosis in the USA, Europe, and Japan?
  • What are the cystinosis marketed drugs and their MOA, regulatory milestones, product development activities, advantages, disadvantages, safety and efficacy, etc.?
  • How many companies are developing therapies for the treatment of cystinosis?
  • How many therapies are developed by each company for cystinosis treatment?
  • How many are emerging therapies in mid-stage, and late stage of development for cystinosis treatment?
  • What are the key collaborations (Industry - Industry, Industry - Academia), Mergers and acquisitions, licensing activities related to the cystinosis therapies?
  • What are the recent novel therapies, targets, mechanisms of action and technologies developed to overcome the limitation of existing therapies?
  • What are the clinical studies going on for cystinosis and their status?
  • What are the key designations that have been granted for the emerging therapies for cystinosis?
  • What are the global historical and forecasted market of cystinosis?

Reasons to buy

  • The report will help in developing business strategies by understanding trends shaping and driving the cystinosis market
  • To understand the future market competition in the cystinosis market and Insightful review of the key market drivers and barriers
  • Organize sales and marketing efforts by identifying the best opportunities for cystinosis in the US, Europe (Germany, Spain, Italy, France, and the United Kingdom) and Japan
  • Identification of strong upcoming players in the market will help in devising strategies that will help in getting ahead of competitors
  • Organize sales and marketing efforts by identifying the best opportunities for cystinosis market
  • To understand the future market competition in the cystinosis market

Table of Contents

1. Key Insights

2. Executive Summary of cystinosis

3. Competitive Intelligence Analysis for cystinosis

4. cystinosis: Market Overview at a Glance

  • 4.1. cystinosis Total Market Share (%) Distribution in 2017
  • 4.2. cystinosis Total Market Share (%) Distribution in 2030

5. cystinosis: Disease Background and Overview

  • 5.1. Introduction
  • 5.2. Sign and Symptoms
  • 5.3. Pathophysiology
  • 5.4. Risk Factors
  • 5.5. Diagnosis

6. Patient Journey

7. cystinosis Epidemiology and Patient Population

  • 7.1. Epidemiology Key Findings
  • 7.2. Assumptions and Rationale: 7MM
  • 7.3. Epidemiology Scenario: 7MM
    • 7.3.1. cystinosis Epidemiology Scenario in the 7MM (2017-2030)
  • 7.4. United States Epidemiology
    • 7.4.1. cystinosis Epidemiology Scenario in the United States (2017-2030)
  • 7.5. EU-5 Country-wise Epidemiology
    • 7.5.1. Germany Epidemiology
      • 7.5.1.1. cystinosis Epidemiology Scenario in Germany (2017-2030)
    • 7.5.2. France Epidemiology
      • 7.5.2.1. cystinosis Epidemiology Scenario in France (2017-2030)
    • 7.5.3. Italy Epidemiology
      • 7.5.3.1. cystinosis Epidemiology Scenario in Italy (2017-2030)
    • 7.5.4. Spain Epidemiology
      • 7.5.4.1. cystinosis Epidemiology Scenario in Spain (2017-2030)
    • 7.5.5. United Kingdom Epidemiology
      • 7.5.5.1. cystinosis Epidemiology Scenario in the United Kingdom (2017-2030)
    • 7.5.6. Japan Epidemiology
      • 7.5.6.1. cystinosis Epidemiology Scenario in Japan (2017-2030)

8. Treatment Algorithm, Current Treatment, and Medical Practices

  • 8.1. cystinosis Treatment and Management
  • 8.2. cystinosis Treatment Algorithm

9. Unmet Needs

10. Key Endpoints of cystinosis Treatment

11. Marketed Products

  • 11.1. List of Marketed Products in the 7MM
  • 11.2. Drug Name: Company Name
    • 11.2.1. Product Description
    • 11.2.2. Regulatory Milestones
    • 11.2.3. Other Developmental Activities
    • 11.2.4. Pivotal Clinical Trials
    • 11.2.5. Summary of Pivotal Clinical Trial

List to be continued in report

12. Emerging Therapies

  • 12.1. Key Cross
  • 12.2. Drug Name: Company Name
    • 12.2.1. Product Description
    • 12.2.2. Other Developmental Activities
    • 12.2.3. Clinical Development
    • 12.2.4. Safety and Efficacy
    • 12.2.5. Product Profile

List to be continued in report

13. cystinosis: Seven Major Market Analysis

  • 13.1. Key Findings
  • 13.2. cystinosis Market Size in 7MM
  • 13.3. cystinosis Market Size by Therapies in the 7MM

14. Attribute analysis

15. 7MM: Market Outlook

  • 15.1. United States: Market Size
    • 15.1.1. cystinosis Total Market Size in the United States
    • 15.1.2. cystinosis Market Size by Therapies in the United States
  • 15.2. EU-5 countries: Market Size and Outlook
  • 15.3. Germany Market Size
    • 15.3.1. cystinosis Total Market Size in Germany
    • 15.3.2. cystinosis Market Size by Therapies in Germany
  • 15.4. France Market Size
    • 15.4.1. cystinosis Total Market Size in France
    • 15.4.2. cystinosis Market Size by Therapies in France
  • 15.5. Italy Market Size
    • 15.5.1. cystinosis Total Market Size in Italy
    • 15.5.2. cystinosis Market Size by Therapies in Italy
  • 15.6. Spain Market Size
    • 15.6.1. cystinosis Total Market Size in Spain
    • 15.6.2. cystinosis Market Size by Therapies in Spain
  • 15.7. United Kingdom Market Size
    • 15.7.1. cystinosis Total Market Size in the United Kingdom
    • 15.7.2. cystinosis Market Size by Therapies in the United Kingdom
  • 15.8. Japan Market Outlook
    • 15.8.1. Japan Market Size
    • 15.8.2. cystinosis Total Market Size in Japan
    • 15.8.3. cystinosis Market Size by Therapies in Japan

16. Access and Reimbursement Overview of cystinosis

17. KOL Views

18. Market Drivers

19. Market Barriers

20. Appendix

  • 20.1. Bibliography
  • 20.2. Report Methodology

21. DelveInsight Capabilities

22. Disclaimer

23. About DelveInsight

List of Tables

  • Table 1 : 7MM cystinosis Epidemiology (2017-2030)
  • Table 2 : 7MM cystinosis Diagnosed and Treatable Cases (2017-2030)
  • Table 3 : Disease% Epidemiology in the United States (2017-2030)
  • Table 4 : cystinosis Diagnosed and Treatable Cases in the United States (2017-2030)
  • Table 5 : cystinosis Epidemiology in Germany (2017-2030)
  • Table 6 : cystinosis Diagnosed and Treatable Cases in Germany (2017-2030)
  • Table 7 : cystinosis Epidemiology in France (2017-2030)
  • Table 8 : cystinosis Diagnosed and Treatable Cases in France (2017-2030)
  • Table 9 : cystinosis Epidemiology in Italy (2017-2030)
  • Table 10 : cystinosis Diagnosed and Treatable Cases in Italy (2017-2030)
  • Table 11 : cystinosis Epidemiology in Spain (2017-2030)
  • Table 12 : cystinosis Diagnosed and Treatable Cases in Spain (2017-2030)
  • Table 13 : cystinosis Epidemiology in the UK (2017-2030)
  • Table 14 : cystinosis Diagnosed and Treatable Cases in the UK (2017-2030)
  • Table 15 : cystinosis Epidemiology in Japan (2017-2030)
  • Table 16 : cystinosis Diagnosed and Treatable Cases in Japan (2017-2030)
  • Table 17 : Drug Name, Clinical Trials by Recruitment status
  • Table 18 : Drug Name, Clinical Trials by Zone
  • Table 19 : Total Seven Major Market Size in USD, Million (2017-2030)
  • Table 20 : Region-wise Market Size in USD, Million (2017-2030)
  • Table 21 : 7MM-Market Size by Therapy in USD, Million (2017-2030)
  • Table 22 : United States Market Size in USD, Million (2017-2030)
  • Table 23 : United States Market Size by Therapy in USD, Million (2017-2030)
  • Table 24 : Germany Market Size in USD, Million (2017-2030)
  • Table 25 : Germany Market Size by Therapy in USD, Million (2017-2030)
  • Table 26 : France Market Size in USD, Million (2017-2030)
  • Table 27 : France Market Size by Therapy in USD, Million (2017-2030)
  • Table 28 : Italy Market Size in USD, Million (2017-2030)
  • Table 29 : Italy Market Size by Therapy in USD, Million (2017-2030)
  • Table 30 : Spain Market Size in USD, Million (2017-2030)
  • Table 31 : Spain Market Size by Therapy in USD, Million (2017-2030)
  • Table 32 : United Kingdom Market Size in USD, Million (2017-2030)
  • Table 33 : United Kingdom Market Size by Therapy in USD, Million (2017-2030)
  • Table 34 : Japan Market Size in USD, Million (2017-2030)
  • Table 35 : Japan Market Size by Therapy in USD, Million (2017-2030)

List of Figures

  • Figure 1 : 7MM cystinosis Epidemiology (2017-2030)
  • Figure 2 : 7MM cystinosis Diagnosed and Treatable Cases (2017-2030)
  • Figure 3 : cystinosis Epidemiology in the United States (2017-2030)
  • Figure 4 : cystinosis Diagnosed and Treatable Cases in the United States (2017-2030)
  • Figure 5 : cystinosis Epidemiology in Germany (2017-2030)
  • Figure 6 : cystinosis Diagnosed and Treatable Cases in Germany (2017-2030)
  • Figure 7 : cystinosis Epidemiology in France (2017-2030)
  • Figure 8 : cystinosis Diagnosed and Treatable Cases in France (2017-2030)
  • Figure 9 : cystinosis Epidemiology in Italy (2017-2030)
  • Figure 10 : cystinosis Diagnosed and Treatable Cases in Italy (2017-2030)
  • Figure 11 : cystinosis Epidemiology in Spain (2017-2030)
  • Figure 12 : cystinosis Diagnosed and Treatable Cases in Spain (2017-2030)
  • Figure 13 : cystinosis Epidemiology in the UK (2017-2030)
  • Figure 14 : cystinosis Diagnosed and Treatable Cases in the UK (2017-2030)
  • Figure 15 : cystinosis Epidemiology in Japan (2017-2030)
  • Figure 16 : cystinosis Diagnosed and Treatable Cases in Japan (2017-2030)
  • Figure 17 : Drug Name, Clinical Trials by Recruitment status
  • Figure 18 : Drug Name, Clinical Trials by Zone
  • Figure 19 : Total Seven Major Market Size in USD, Million (2017-2030)
  • Figure 20 : Region-wise Market Size in USD, Million (2017-2030)
  • Figure 21 : 7MM-Market Size by Therapy in USD, Million (2017-2030)
  • Figure 22 : United States Market Size in USD, Million (2017-2030)
  • Figure 23 : United States Market Size by Therapy in USD, Million (2017-2030)
  • Figure 24 : Germany Market Size in USD, Million (2017-2030)
  • Figure 25 : Germany Market Size by Therapy in USD, Million (2017-2030)
  • Figure 26 : France Market Size in USD, Million (2017-2030)
  • Figure 27 : France Market Size by Therapy in USD, Million (2017-2030)
  • Figure 28 : Italy Market Size in USD, Million (2017-2030)
  • Figure 29 : Italy Market Size by Therapy in USD, Million (2017-2030)
  • Figure 30 : Spain Market Size in USD, Million (2017-2030)
  • Figure 31 : Spain Market Size by Therapy in USD, Million (2017-2030)
  • Figure 32 : United Kingdom Market Size in USD, Million (2017-2030)
  • Figure 33 : United Kingdom Market Size by Therapy in USD, Million (2017-2030)
  • Figure 34 : Japan Market Size in USD, Million (2017-2030)
  • Figure 35 : Japan Market Size by Therapy in USD, Million (2017-2030)